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Kren, B.T., Unger, G.M., Sjeklocha, L., Trossen, A.A., Korman, V., Diethelm-Okita, B.M., Reding, M.T. and Steer, C.J. (2009) Nanocapsule-delivered Sleeping Beauty mediates therapeutic Factor VIII expression in liver sinusoidal endothelial cells of hemophilia A mice. Journal of Clinical Investigation, 119, 2086-2099.
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